Back to News Back to Stories Impact of long-term elosulfase alfa treatment on clinical and patient-reported outcomes in patients with mucopolysaccharidosis type IVA: results from a Managed Access Agreement in England January 21, 2021
Community A 100-Mile Road to Diagnosis: A Mother Shares Her Son’s Journey with Hypochondroplasia March 14, 2024
People and Culture Supporting Women at 博彩平台网址大全: An Interview with the Co-Chairs of Our Women’s Leadership Development Group March 8, 2024
Community Caring for Children with Achondroplasia: An Interview with Dr. Ciara McDonnell October 25, 2023
Community RARE Scholars Program Provides Support to College Students Living with Genetic Conditions September 25, 2023
People and Culture Science 博彩平台网址大全 Teams Use Genetic Expertise and Computational Tools to Target More Common Conditions September 8, 2023
Community People and Culture Raising a Child with Hemophilia: 博彩平台网址大全 Employee Jess Klass Shares Her Story July 21, 2023
